Effectiveness and safety of azathioprine for inflammatory pouch disorders: results from the RESERVO study of GETECCU


Por: Mesonero, F, Zabana, Y, Fernández-Clotet, A, Leo-Carnerero, E, Caballol, B, Núñez-Ortiz, A, García, MJ, Bertoletti, F, Mínguez, A, Suris, G, Casis, B, Ferreiro-Iglesias, R, Calafat, M, Jiménez, I, Miranda-Bautista, J, Lamuela, LJ, Fajardo, I, Torrealba, L, Nájera, R, Saíz-Chumillas, RM, González, I, Vicuña, M, García-Morales, N, Gutiérrez, A, López-García, A, Benítez, JM, de Célix, CR, Tejido, C, Brunet, E, Hernández-Camba, A, Suárez, C, Rodríguez-Lago, I, Piqueras, M, Castaño, A, Ramos, L, Sobrino, A, Rodríguez-Grau, MC, Elosua, A, Montoro, M, Baltar, R, Huguet, JM, Hermida, B, Caballero-Mateos, A, Sánchez-Guillén, L, Bouhmidi, A, Pajares, R, Baston-Rey, I, López-Sanromán, A, Albillos, A and Barreiro-de Acosta, M

Publicada: 1 ene 2024
Resumen:
Background: The usefulness of thiopurines has been poorly explored in pouchitis and other pouch disorders.Objective: To evaluate the effectiveness and safety of azathioprine as maintenance therapy in inflammatory pouch disorders.Design: This was a retrospective and multicentre study.Methods: We included patients diagnosed with inflammatory pouch disorders treated with azathioprine in monotherapy. Effectiveness was evaluated at 1 year and in the long term based on normalization of stool frequency, absence of pain, faecal urgency or fistula discharge (clinical remission), or any improvement in these symptoms (clinical response). Endoscopic response was evaluated using the Pouchitis Disease Activity Index (PDAI).Results: In all, 63 patients were included [54% males; median age, 49 (28-77) years]. The therapy was used to treat pouchitis (n = 37) or Crohn's disease of the pouch (n = 26). The rate of clinical response, remission and non-response at 12 months were 52%, 30% and 18%, respectively. After a median follow-up of 23 months (interquartile range 11-55), 19 patients (30%) were in clinical remission, and 45 (66%) stopped therapy. Endoscopic changes were evaluated in 19 cases. PDAI score decreased from 3 (range 2-4) to 1 (range 0-3). In all, 21 patients (33%) presented adverse events and 16 (25%) needed to stop therapy.Conclusion: Azathioprine may be effective in the long term for the treatment of inflammatory pouch disorders and could be included as a therapeutic option.

Filiaciones:
Mesonero, F:
 Hosp Univ Ramon Y Cajal, Dept Gastroenterol & Hepatol, Inflammatory Bowel Dis Unit, Cra Colmenar Km 9-1, Madrid 28034, Spain

Zabana, Y:
 Hosp Univ Mutua Terrassa, Terrassa, Spain

 Ctr Invest Biomed Red Enfermedades Hepat & Digest, Madrid, Spain

Fernández-Clotet, A:
 Ctr Invest Biomed Red Enfermedades Hepat & Digest, Madrid, Spain

 Hosp Clin Barcelona, Inst Invest Biomed August Pi & Sunyer IDIBAPS, Barcelona, Spain

Leo-Carnerero, E:
 Hosp Univ Virgen Rocio, Seville, Spain

Caballol, B:
 Ctr Invest Biomed Red Enfermedades Hepat & Digest, Madrid, Spain

 Hosp Clin Barcelona, Inst Invest Biomed August Pi & Sunyer IDIBAPS, Barcelona, Spain

Núñez-Ortiz, A:
 Hosp Univ Virgen Rocio, Seville, Spain

García, MJ:
 Hosp Univ Marques de Valdecilla, IDIVAL, Santander, Spain

Bertoletti, F:
 Hosp Santa Creu & Sant Pau, Barcelona, Spain

Mínguez, A:
 Hosp Univ & Politecn La Fe, Valencia, Spain

Suris, G:
 Hosp Univ Bellvitge, Barcelona, Spain

Casis, B:
 Hosp Univ 12 Octubre, Madrid, Spain

Ferreiro-Iglesias, R:
 Hosp Clin Univ Santiago, Santiago De Compostela, Spain

:
 Ctr Invest Biomed Red Enfermedades Hepat & Digest, Madrid, Spain

 Hosp Badalona Germans Trias & Pujol, Badalona, Spain

Jiménez, I:
 Hosp Univ Galdakao, Biocruces Bizkaia Hlth Res Inst, Galdakao, Spain

Miranda-Bautista, J:
 Hosp Univ Gregorio Maranon, Madrid, Spain

Lamuela, LJ:
 Hosp Univ Miguel Servet, Zaragoza, Spain

Fajardo, I:
 Hosp Univ Mutua Terrassa, Terrassa, Spain

Torrealba, L:
 Hosp Univ Doctor Josep Trueta, Girona, Spain

Nájera, R:
 Hosp Univ Rio Hortega, Valladolid, Spain

Saíz-Chumillas, RM:
 Hosp Univ Burgos, Burgos, Spain

González, I:
 Hosp Univ Puerta Hierro, Madrid, Spain

Vicuña, M:
 Complejo Hosp Navarra, Pamplona, Spain

García-Morales, N:
 Hosp Alvaro Cunqueiro, Vigo, Spain

Gutiérrez, A:
 Ctr Invest Biomed Red Enfermedades Hepat & Digest, Madrid, Spain

 Hosp Gen Univ Alicante Doctor Balmis Alicante, Inst Invest Sanitaria & Biomed Alicante ISABIAL, Alicante, Spain

López-García, A:
 Hosp del Mar, Barcelona, Spain

 Inst Mar Invest Med IMIM, Barcelona, Spain

Benítez, JM:
 Hosp Univ Reina Sofia, Cordoba, Spain

de Célix, CR:
 Ctr Invest Biomed Red Enfermedades Hepat & Digest, Madrid, Spain

 Hosp Univ Princesa, Univ Autonoma Madrid UAM, Inst Invest Sanitaria Princesa IIS Princesa, Madrid, Spain

Tejido, C:
 Complejo Hosp Univ Ourense, Orense, Spain

Brunet, E:
 Ctr Invest Biomed Red Enfermedades Hepat & Digest, Madrid, Spain

 Hosp Univ Parc Tauli, Sabadell, Spain

Hernández-Camba, A:
 Hosp Univ Nuestra Senora Candelaria, Santa Cruz de La Palma, Spain

Suárez, C:
 Hosp Univ La Paz, Inst Invest Sanitaria Hosp Univ La Paz IdiPAZ, Madrid, Spain

Rodríguez-Lago, I:
 Hosp Univ Galdakao, Biocruces Bizkaia Hlth Res Inst, Galdakao, Spain

Piqueras, M:
 Consorcio Sanitario Terrassa, Terrassa, Spain

Castaño, A:
 Hosp Univ Cent Asturias, Oviedo, Spain

Ramos, L:
 Hosp Univ Canarias, Santa Cruz de La Palma, Spain

Sobrino, A:
 Hosp Gen Univ Ciudad Real, Ciudad Real, Spain

Rodríguez-Grau, MC:
 Hosp Univ Henares, Coslada, Spain

Elosua, A:
 Hosp Garcia Orcoyen, Estella, Spain

Montoro, M:
 Hosp Gen Univ San Jorge, Huesca, Spain

Baltar, R:
 Hosp Univ Alava, Vitoria, Spain

Huguet, JM:
 Hosp Gen Univ Valencia, Valencia, Spain

Hermida, B:
 Hosp Univ Cabuenes, Gijon, Spain

Caballero-Mateos, A:
 Hosp Santa Ana Motril, Motril, Spain

Sánchez-Guillén, L:
 Hosp Gen Univ Elche, Elche, Spain

Bouhmidi, A:
 Hosp Santa Barbara, Puertollano, Spain

Pajares, R:
 Hosp Univ Infanta Sofia, San Sebastian De Los Reye, Spain

Baston-Rey, I:
 Hosp Clin Univ Santiago, Santiago De Compostela, Spain

López-Sanromán, A:
 Hosp Univ Ramon & Cajal, Madrid, Spain

Albillos, A:
 Hosp Univ Ramon & Cajal, Madrid, Spain

Barreiro-de Acosta, M:
 Hosp Clin Univ Santiago, Santiago De Compostela, Spain
ISSN: 17562848





Therapeutic Advances in Gastroenterology
Editorial
SAGE Publications, 1 OLIVERS YARD, 55 CITY ROAD, LONDON EC1Y 1SP, ENGLAND, Reino Unido
Tipo de documento: Article
Volumen: 17 Número:
Páginas:
WOS Id: 001183492000001
ID de PubMed: 38445247
imagen Green Published, gold

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