Blinatumomab vs historic standard-of-care treatment for minimal residual disease in adults with B-cell precursor acute lymphoblastic leukaemia


Por: Gokbuget, N, Dombret, H, Giebel, S, Bruggemann, M, Doubek, M, Foa, R, Hoelzer, D, Kim, C, Martinelli, G, Parovichnikova, E, Ribera, JM, Schoonen, M, Tuglus, C, Zugmaier, G and Bassan, R

Publicada: 1 abr 2020 Ahead of Print: 1 ene 2020
Resumen:
Objectives Survival outcomes from a single-arm phase 2 blinatumomab study in patients with minimal residual disease (MRD)-positive B-cell precursor (BCP)-acute lymphoblastic leukaemia (ALL) were compared with those receiving standard of care (SOC) in a historic data set. Methods The primary analysis comprised adult Philadelphia chromosome (Ph)-negative patients in first complete haematologic remission (MRD >= 10(-3)). Relapse-free survival (RFS) and overall survival (OS) were compared between blinatumomab- and SOC-treatment groups. Baseline differences between groups were adjusted by propensity scores. Results The primary analysis included 73 and 182 patients from the blinatumomab and historic data sets, respectively. When weighted by age to the blinatumomab-treatment group, median RFS was 7.8 months and median OS was 25.9 months in the SOC-treated group. In the blinatumomab study, median RFS was 35.2 months; median OS was not evaluable. Propensity score weighting achieved balance with seven baseline prognostic factors. With adjustment for haematopoietic stem cell transplantation (HSCT) status, a 50% reduction in risk of relapse or death was observed with blinatumomab vs SOC. Median RFS, unadjusted for HSCT status, was 35.2 months with blinatumomab and 8.3 months with SOC. Conclusions These analyses suggest that blinatumomab improves RFS, and possibly OS, in adults with MRD-positive Ph-negative BCP-ALL vs SOC.

Filiaciones:
Gokbuget, N:
 Goethe Univ, Univ Hosp, Frankfurt, Germany

Dombret, H:
 Univ Paris Diderot, Hop St Louis, Paris, France

Giebel, S:
 Maria Sklodowska Curie Inst, Oncol Ctr, Gliwice, Poland

Bruggemann, M:
 Univ Hosp Schleswig Holstein, Kiel, Germany

Doubek, M:
 Univ Hosp, Brno, Czech Republic

 Masaryk Univ, CEITEC, Brno, Czech Republic

Foa, R:
 Sapienza Univ Rome, Rome, Italy

Hoelzer, D:
 JW Goethe Univ Hosp, Frankfurt, Germany

Kim, C:
 Amgen Inc, Ctr Observat Res, Thousand Oaks, CA 91320 USA

Martinelli, G:
 Policlin S Orsola Ist Seragnoli, Bologna, Italy

Parovichnikova, E:
 Natl Res Ctr Hematol, Moscow, Russia

:
 Hosp Badalona Germans Trias & Pujol, Jose Carreras Res Inst, ICO, Barcelona, Spain

Schoonen, M:
 Amgen Ltd, Ctr Observat Res, Uxbridge, Middx, England

Tuglus, C:
 Amgen Inc, Biostat, Thousand Oaks, CA 91320 USA

Zugmaier, G:
 Amgen Europe GmbH, Clin Dev, Munich, Germany

Bassan, R:
 Osped Angelo, UOC Ematol, Mestre Venezia, Italy
ISSN: 09024441





European Journal of Haematology
Editorial
Blackwell Publishing Inc., 111 RIVER ST, HOBOKEN 07030-5774, NJ USA, Reino Unido
Tipo de documento: Article
Volumen: 104 Número: 4
Páginas: 299-309
WOS Id: 000509095600001
ID de PubMed: 31876009
imagen Green Published, hybrid

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